Molecular Med TriCon 2019 | Gene Therapy for Rare Disorders


Manage episode 248298673 series 31038
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Gene therapy presents a promising path ahead for patients of rare diseases. The United States Food and Drug Administration’s Director of the Center for Biologics Evaluation and Research, Dr. Peter Marks discusses his work advancing production and availability of gene therapies for rare disorders, and the unique challenges to producing efficacious therapeutics in this field. For more information, please visit

255 episodes